New collaboration aims to research early mutations in rare blood disorder
Langerhans cell histiocytosis currently affects around one in 200,000 children in the UK
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Tag: rare blood disorder
NICE publish final guidance recommending Aspaveli in adults with ultra-rare blood disorder
The drug is additionally undergoing assessment with the Medicines and Healthcare products Regulatory Agency for a marketing authorisation in the UK
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- Kainova reports positive results for DT‑9081 in advanced solid tumours
- EnteroBiotix completes enrolment for trial of EBX‑102‑02
- Lundbeck completes patient randomisation early in global MSA trial
- Incyte treatment for advanced anal cancer approved in Europe
- HUTCHMED begins global trial of novel attc therapy hmpl‑a580 in solid tumours
