Kuvan approved for pregnant women with PKU in UK
NICE decision also extends treatment to people aged up to 22 years old
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Tag: PKU
‘Innovative’ PKU treatment launched in UK
PKU is a rare, inherited metabolic disorder that affects approximately 70 babies each year in the UK.
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US clears first enzyme therapy for PKU
Biomarin’s Palynziq has been approved as the first enzyme therapy to treat the rare brain-threatening genetic disease phenylketonuria (PKU) in adults in the US.
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