Tag: Mepsevii

EU OKs first treatment for ultra rare lysosomal storage disorder

by Selina McKee | Aug 29, 2018 | News | 0

Ultragenyx’ Mepsevii has been cleared for use in Europe to treat the ultra rare disease mucopolysaccharidosis type VII (MPS VII), offering patients an approved treatment for the very first time.

CAR-T therapies leap towards EU approval

by Selina McKee | Jul 2, 2018 | News | 0

The stage has been set for approval of the first chimeric antigen T-cell therapies (CAR-T) in Europe, after Novartis’ Kymriah and Gilead’s Yescarta both won backing from the Committee for Medicinal Products for Human Use (CHMP).