UK’s MHRA allows early access to lumasiran for ultra-rare disease
Lumasiran targets primary hyperoxaluria type 1 (PH1), which affects just around 90 people in the UK and one to three individuals per million in Europe
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Tag: lumasiran
Alynlam completes EU, US filings for lumasiran
If approved, lumasiran would be the first approved therapeutic treatment option for primary hyperoxaluria type 1
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