Alexion Pharma and the National Institute for Health and Care Excellence have come to a new arrangement that widens NHS access to Strensiq for people with paediatric-onset hypophosphatasia.
The National Institute for Health and Care Excellence has published draft guidelines that restrict the use of Alexion’s £366,912-a-year enzyme replacement therapy Strensiq by the National Health Service in treating patients with hypophosphatasia.
Cost regulators for NHS treatments in England and Wales have recommended use of Alexion’s Strensiq to treat a rare and often fatal condition called hypophosphatasia (HPP), but have restricted its reach to children with certain forms of the condition.