The drug is used to treat seizures caused by this rare syndrome that is a form of epilepsy
News
Sandoz launches new global health inequalities initiative
‘Act4Biosimilars’ will improve patient access and increase adoption in over 30 countries by 2030
Memo Therapeutics initiates pioneering BK virus therapy trial
Antibody addresses high unmet medical need in rapidly growing kidney transplant market
NICE approves Merck’s Keytruda for adult patients with rare triple negative breast cancer
The injection is given in combination with chemotherapy and administered once every three weeks
NRG receives £2.68m funding boost for neurodegenerative disorders
NRG Therapeutics announces multi-million Innovate UK Award to develop treatments for Parkinson’s and motor neurone disease
Thousands to potentially benefit from Roche treatment for sight loss
Faricimab is administered as an eye injection with an interval of up to 16 weeks
AstraZeneca kidney inflammation treatment trial reaches dosing stage
Initial group of patients have received Saphnelo in a phase 3 trial evaluating lupus nephritis
NICE recommendation for Sanofi and Regeneron’s CSCC treatment
Libtayo has been approved for adults when curative surgery or radiation is not appropriate
EC approves Janssen T-cell therapy for multiple myeloma treatment
Approval provides another step forward in transforming multiple myeloma outcomes and eliminating the disease
Cumulus Neuroscience begins studies of digital biomarker
Technology is already being used in clinical trials of new treatments for Alzheimer’s and new studies will provide additional validation
Pfizer/BioNTech vaccine effective against Omicron in children five and under
Companies say that three-dose vaccine for children aged six months to five years old is 80% effective at preventing illness
Alternative to open heart surgery emerges following NIHR research
Less invasive procedure offers an equally effective alternative for heart condition patients
PTC Therapeutic’s Upstaza has been recommended by both the EMA and CHMP
It is the first gene therapy to be directly administered into the brain to treat aromatic L-amino acid decarboxylase (AADC) deficiency
CHMP recommends Sanofi’s Xenpozyme for rare disease ASMD
Positive opinion is based on data from clinical trials which showed improvement in lung function
NICE recommends app-based treatment for insomnia over sleeping pills
Thousands usually prescribed sleeping pills could be offered app-based treatment
